Your Monthly Medicines Roundup for January 2024

Your Monthly Medicines Roundup for January 2024

Well, January’s flown hasn’t it?

This has been a busy month for medicines and two medicines were approved for the treatment of some inherited metabolic disorders (IMDs).

You can find a round-up of all approved medicines, alphabetised by disorder name below:  

Wolman disease

Sebelipase alfa has been approved long-term enzyme replacement therapy for people who are aged 2 years and under when treatment starts. This type of medical treatment replaces an enzyme that is deficient or absent in the body and was approved by the National Institute for Health and Care Excellence (NICE) in England.

For further details, click the button below:

X-linked hypophosphatemia

Burosumab has been approved for the treatment of X-linked hypophosphataemia in children and adolescents aged 1 to 17 years with radiographic evidence of bone disease. This treatment improves bone mineralisation to decrease the effects of bone diseases and was approved for use within NHS Scotland by the Scottish Medicines Consortium (SMC).

For further details, click the button below:

Skip to content